Zydus gets Orphan Drug Designation from USFDA for ZYIL1 to treat Cryopyrin Associated Periodic Syndrome Read more
US FDA grants Orphan Drug Designation to BCMA CAR-T cell therapy co-developed by Innovent Biologics and IASO Bio Read more
Theseus Pharmaceuticals receives US FDA Orphan Drug Designation for THE-630 to treat Advanced Gastrointestinal Stromal Tumours (GIST) Read more
US FDA grants Orphan Drug Designation to Zydus’ Saroglitazar for primary biliary cholangitis treatment Read more
TSHA-102 from Taysha gets rare paediatric disease and orphan drug designations for Rett syndrome Read more