Givinostat from Italfarmaco gets FDA rare pediatric disease designation in duchenne muscular dystrophy Read more
Kyowa Kirin gets EC approval for CRYSVITA (burosumab) to treat X-Linked hypophosphataemia in older adolescents and adults Read more
Pfizer get USFDA nod for XELJANZ (tofacitinib) to treat active polyarticular course juvenile idiopathic arthritis Read more